First Patient in the World Treated With Gene Therapy for Cockayne Syndrome

Riaan Singh Digeorge, age 6, of New York City, received an experimental AAV9 gene therapy for Cockayne syndrome following a historic parent-led drug development effort by Riaan Research Initiative. NEW YORK, June 22, 2026 /PRNewswire/ -- Riaan Research Initiative (RRI), a rare disease...